The Role of CRISPR and AAV in Duchenne Gene Repair

σε πρόσθεσε στο Health

2025-06-17 07:02:31

Duchenne Muscular Dystrophy (DMD) is a rare, progressive neuromuscular disorder that leads to severe muscle degeneration and early mortality. Affecting roughly 1 in 3,500 to 5,000 male births globally, DMD stems from mutations in the DMD gene, which encodes dystrophin, a protein critical for muscle fiber integrity. Without dystrophin, muscle cells become fragile and eventually die, leading to...

0 Σχόλια 0 Μοιράστηκε 84 Views 0 Προεπισκόπηση