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Paroxysmal Nocturnal Hemoglobinuria Market – DelveInsight Perspective
Paroxysmal Nocturnal Hemoglobinuria (PNH) is a rare but life-threatening blood disorder caused by acquired mutations in the PIGA gene. These mutations result in the loss of complement regulators on red blood cells, triggering uncontrolled complement activity. The condition is marked by chronic hemolysis (both intravascular and extravascular), severe fatigue, anemia, smooth-muscle complications,...
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