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Mucopolysaccharidosis I Market Report Compiled by DelveInsight
Mucopolysaccharidosis I (MPS I) stands as a rare inherited metabolic disorder caused by deficient alpha-L-iduronidase enzyme activity, leading to harmful glycosaminoglycan deposits throughout various body tissues. The treatment sector for this uncommon genetic condition has witnessed remarkable progress over recent years, fueled by innovations in enzyme therapy protocols, stem cell...
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